Concepedia

Long-term efficacy of hematopoietic stem cell transplantation on brain involvement in patients with mucopolysaccharidosis type II: A nationwide survey in Japan

Akemi Tanaka, Torayuki Okuyama, Yasuyuki Suzuki, Norio Sakai, Hiromitsu Takakura, Tomo Sawada, Toju Tanaka, Takanobu Otomo, Toya Ohashi, Mika Ishige-Wada,

Molecular Genetics and Metabolism · 2012 · 147 citations · 24 references

Concepts

MedicineHematologyNeurologyClinical NeuroscienceStem Cell TransplantationHematopoietic Stem Cell TransplantationHematopoietic Stem Cell Transplantation ImmunotherapyLong-term Efficacy AssessmentLong-term Efficacy EvaluationNeurologic Complications After Transplantation

References

24

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

Nathalie Cartier, Salima Hacein‐Bey‐Abina, Cynthia C. Bartholomae et al. · Science · 2009 · 1.5K citations · Full text

Medicine, Neurology, Neuroscience +17

Left retrograde cardioangiography in acquired cardiac disease

Robert D. Sellers, Morris J. Levy, Kurt Amplatz et al. · The American Journal of Cardiology · 1964 · 803 citations

Medicine, Cardiology, Radiology +6

REVERSAL OF CLINICAL FEATURES OF HURLER'S DISEASE AND BIOCHEMICAL IMPROVEMENT AFTER TREATMENT BY BONE-MARROW TRANSPLANTATION

Jacqueline A. Hobbs · The Lancet · 1981 · 494 citations

Medicine, Hematology, Stem Cell Transplantation +6

Cord-Blood Transplants from Unrelated Donors in Patients with Hurler's Syndrome

Susan Staba, Maria L. Escolar, Michele D. Poe et al. · New England Journal of Medicine · 2004 · 481 citations · Full text

Medicine, Hematology, Pediatrics +17

Mucopolysaccharidosis I: Management and Treatment Guidelines

Joseph Muenzer, J. E. Wraith, L. Clarke · PEDIATRICS · 2008 · 460 citations

Medicine, Hematology, Pediatrics +10