Molecular Therapy · 2012 · 23 citations · 48 references
PharmacyMolecular MedicineTranslational SciencesGene TherapyMolecular VirologyStem Cell TransplantationAntiviral PharmacotherapyAntiviral TherapyGene Delivery To Stem CellsGene Delivery VectorsStem Cell Gene TherapyViral Vector-mediated TransgenesisAutologous EngraftmentHerpesvirus VectorsPrimary Immunodeficiency DisordersPrimary Immunodeficiency Gene TherapyProgenitor CellsRetroviral VectorsTherapeutic Gene TransferViral Vectors
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Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
Marina Cavazzana, Salima Hacein‐Bey, Geneviève de Saint Basile et al. · Science · 2000 · 2.6K citations
Life Sciences, Genetics, Immunology +17
Inducible Apoptosis as a Safety Switch for Adoptive Cell Therapy
Antonio Di Stasi, Siok‐Keen Tey, Gianpietro Dotti et al. · New England Journal of Medicine · 2011 · 1.5K citations · Full text