Publication | Open Access
RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
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2013
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Rna ToxicityEngineeringRna BiologyMolecular BiologyAntisense TherapySystems BiologyMedicineGene ExpressionGenome EditingAntisense InterventionNon-coding Rna
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