Parent Project Onlus

The TREAT-NMD DMD Global Database: Analysis of More than 7,000 Duchenne Muscular Dystrophy Mutations

Catherine L. Bladen, David Salgado, Soledad Monges et al. · Human Mutation · 2015 · 744 citations · Full text

Life Sciences, Genetics, Molecular Genetics +15

Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database

Zaïda Koeks, Catherine L. Bladen, David Salgado et al. · Journal of Neuromuscular Diseases · 2017 · 182 citations · Full text

Medicine, Neurology, Clinical Epidemiology +4

Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study

Eugenio Mercuri, Francesco Muntoni, A. Nascimento Osorio et al. · Journal of Comparative Effectiveness Research · 2020 · 126 citations · Full text

Medicine, Translational Sciences, Clinical Epidemiology +12

The TREAT-NMD Duchenne Muscular Dystrophy Registries: Conception, Design, and Utilization by Industry and Academia

Catherine L. Bladen, Karen Rafferty, Volker Straub et al. · Human Mutation · 2013 · 108 citations

Medicine, Neurology, Good Clinical Practice +13

Safety and effectiveness of ataluren in patients with nonsense mutation DMD in the STRIDE Registry compared with the CINRG Duchenne Natural History Study (2015–2022): 2022 interim analysis

Eugenio Mercuri, A. Nascimento Osorio, Francesco Muntoni et al. · Journal of Neurology · 2023 · 44 citations · Full text

Medicine, Genetics, Neurology +14