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Robert J. Adams, Lewis L. Hsu, Elliott Vichinsky et al. · New England Journal of Medicine · 1998 · 1.9K citations · Full text
Medicine, Hematology, Pediatrics +10
Michelle M. Clark, Zornitza Stark, Lauge Farnaes et al. · npj Genomic Medicine · 2018 · 640 citations · Full text
Life Sciences, Genetics, Pediatrics +17
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