Aurélie Barrière

Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study

Claudia A. Chiriboga, Claudio Bruno, Tina Duong et al. · Neurology and Therapy · 2023 · 54 citations · Full text

Medicine, Neurology, Pharmacology +16

A Patient-Centered Evaluation of Meaningful Change on the 32-Item Motor Function Measure in Spinal Muscular Atrophy Using Qualitative and Quantitative Data

Tina Duong, Hannah Staunton, Jessica Braid et al. · Frontiers in Neurology · 2022 · 26 citations · Full text

Medicine, Neurology, Rehabilitation Medicine +16

Understanding the relationship between the 32-item motor function measure and daily activities from an individual with spinal muscular atrophy and their caregivers’ perspective: a two-part study

Tina Duong, Jessica Braid, Hannah Staunton et al. · BMC Neurology · 2021 · 18 citations · Full text

Medicine, Neurology, Rehabilitation Medicine +17