B C Y Au

Systemic ceramide accumulation leads to severe and varied pathological consequences

Abdulfatah M. Alayoubi, James C.M. Wang, B C Y Au et al. · EMBO Molecular Medicine · 2013 · 105 citations · Full text

Medicine, Oncology, Pathobiology +11

Lentivector Iterations and Pre-Clinical Scale-Up/Toxicity Testing: Targeting Mobilized CD34 + Cells for Correction of Fabry Disease

Ju Huang, B C Y Au, Dwayne L. Barber et al. · Molecular Therapy — Methods & Clinical Development · 2017 · 46 citations · Full text

Pharmacy, Cell Biology, Molecular Biology +17

Lentivector Transduction Improves Outcomes Over Transplantation of Human HSCs Alone in NOD/SCID/Fabry Mice

Natalia Pacienza, Makoto Yoshimitsu, Nobuo Mizue et al. · Molecular Therapy · 2012 · 25 citations · Full text

Pharmacy, Biochemistry, Cell Biology +13

Engineered human Tmpk fused with truncated cell-surface markers: versatile cell-fate control safety cassettes

Matthew Scaife, Natalia Pacienza, B C Y Au et al. · Gene Therapy · 2012 · 21 citations · Full text

Life Sciences, Biotechnology, Cell Biology +9

Preclinical validation: LV/IL-12 transduction of patient leukemia cells for immunotherapy of AML

Ju Huang, Yuanfeng Liu, B C Y Au et al. · Molecular Therapy — Methods & Clinical Development · 2016 · 20 citations · Full text

Medicine, Immunology, Oncology +13