Gary Elfring

Irinotecan plus Fluorouracil and Leucovorin for Metastatic Colorectal Cancer

Leonard B. Saltz, John V. Cox, Charles D. Blanke et al. · New England Journal of Medicine · 2000 · 3K citations · Full text

Medicine, Oncology, Pharmacology +13

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Craig M. McDonald, Craig Campbell, Ricardo Erazo Torricelli et al. · The Lancet · 2017 · 455 citations · Full text

Medicine, Molecular Medicine, Neurology +9

Ataluren treatment of patients with nonsense mutation dystrophinopathy

K. Bushby, Richard S. Finkel, Brenda Wong et al. · Muscle & Nerve · 2014 · 426 citations · Full text

Medicine, Genetics, Molecular Genetics +17

The 6‐minute walk test as a new outcome measure in Duchenne muscular dystrophy

Craig M. McDonald, Erik Henricson, Jay J. Han et al. · Muscle & Nerve · 2009 · 390 citations

Medicine, Physical Medicine, Rehabilitation Medicine +17

Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial

Eitan Kerem, Samit Hirawat, S. Armoni et al. · The Lancet · 2008 · 387 citations

Life Sciences, Genetics, Molecular Genetics +10