M A Morsy

Efficient adenoviral-mediated ornithine transcarbamylase expression in deficient mouse and human hepatocytes.

M A Morsy, E L Alford, Andrew Bett et al. · Journal of Clinical Investigation · 1993 · 82 citations · Full text

Otc Deficiency, Adenoviral Vector, Hepatology +11

Leptin gene therapy and daily protein administration: a comparative study in the ob/ob mouse

M A Morsy, MC Gu, JZ Zhao et al. · Gene Therapy · 1998 · 43 citations

Knockout Mouse, Gene Therapies, Neuropeptides +10

Patient selection may affect gene therapy success. Dominant negative effects observed for ornithine transcarbamylase in mouse and human hepatocytes.

M A Morsy, Jing Zhao, Thuan-Ethan Ngo et al. · Journal of Clinical Investigation · 1996 · 29 citations · Full text

In Vivo Gene Therapy, Patient Selection, Genetics +22

P3.51 Results of a Phase 2b, dose-ranging study of ataluren (PTC124®) in nonsense mutation Duchenne/Becker muscular dystrophy (nmDBMD)

Richard S. Finkel, Brenda Wong, K. Bushby et al. · Neuromuscular Disorders · 2010 · 14 citations

P3.51 Results, Rare Diseases, Mendelian Disorder +9

Preimplantation genetic analysis.

Ra. Kaufmann, M A Morsy, Kazuhiro Takeuchi et al. · PubMed · 1992 · 13 citations

Genetic Testing, Fertility, Genetics +24