Stefán Karlsson

Retroviral Transfer of the Glucocerebrosidase Gene into CD34 ⁺ Cells from Patients with Gaucher Disease: <i>In Vivo</i> Detection of Transduced Cells without Myeloablation

Cynthia E. Dunbar, Donald B. Kohn, Raphael Schiffmann et al. · Human Gene Therapy · 1998 · 174 citations

Medicine, Biotechnology, Hematology +17

Effective cell and gene therapy in a murine model of Gaucher disease

Ida Enquist, Eva Nilsson, Andreas Ooka et al. · Proceedings of the National Academy of Sciences · 2006 · 134 citations · Full text

Life Sciences, Genetics, Molecular Biology +15

Decreased metastatic spread in mice homozygous for a null allele of the cystatin C protease inhibitor gene.

Chang-Goo Huh, Katarina Håkansson, Carl‐Michael Nathanson et al. · Molecular Pathology · 1999 · 132 citations · Full text

Medicine, Genetics, Oncology +11

Correction of glucocerebrosidase deficiency after retroviral-mediated gene transfer into hematopoietic progenitor cells from patients with Gaucher disease.

John K. Fink, P H Correll, Libby Perry et al. · Proceedings of the National Academy of Sciences · 1990 · 89 citations

Life Sciences, Genetics, Molecular Biology +13

Production of glycosylated physiologically "normal" human alpha 1-antitrypsin by mouse fibroblasts modified by insertion of a human alpha 1-antitrypsin cDNA using a retroviral vector.

Robert I. Garver, Anna Chytil, Stefán Karlsson et al. · Proceedings of the National Academy of Sciences · 1987 · 71 citations · Full text

Life Sciences, Genetics, Molecular Biology +13