Brenda Koniar

Prolonged expression of a lysosomal enzyme in mouse liver after <i>Sleeping Beauty</i> transposon‐mediated gene delivery: implications for non‐viral gene therapy of mucopolysaccharidoses

Elena L. Aronovich, Jason Bell, Lalitha R. Belur et al. · The Journal of Gene Medicine · 2007 · 104 citations

Life Sciences, Biotechnology, Genetics +13

Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human α-l-iduronidase gene

Seth D. Hartung, Joel L. Frandsen, Dao Pan et al. · Molecular Therapy · 2004 · 99 citations · Full text

Pharmacy, Biotechnology, Molecular Biology +17

Systemic Correction of Storage Disease in MPS I NOD/SCID Mice Using the Sleeping Beauty Transposon System

Elena L. Aronovich, Jason Bell, Shaukat Khan et al. · Molecular Therapy · 2009 · 87 citations · Full text

Life Sciences, Genetics, Molecular Genetics +10

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

Li Ou, Russell C. DeKelver, Michelle Rohde et al. · Molecular Therapy · 2018 · 85 citations · Full text

Life Sciences, Genetics, Molecular Genetics +14

Co-delivery of natural metabolic inhibitors in a self-microemulsifying drug delivery system for improved oral bioavailability of curcumin

Alex E. Grill, Brenda Koniar, Jayanth Panyam · Drug Delivery and Translational Research · 2014 · 66 citations · Full text

Pharmacy, Pharmaceutics, Pharmacology +13