Sofia E. Luna

Aberrant activation of TCL1A promotes stem cell expansion in clonal haematopoiesis

Joshua S. Weinstock, Jayakrishnan Gopakumar, Bala Bharathi Burugula et al. · Nature · 2023 · 106 citations · Full text

Life Sciences, Cell Biology, Hematology +16

High-efficiency transgene integration by homology-directed repair in human primary cells using DNA-PKcs inhibition

Sridhar Selvaraj, William N. Feist, Sébastien Viel et al. · Nature Biotechnology · 2023 · 102 citations · Full text

Life Sciences, Genetics, Molecular Biology +16

A simultaneous knockout knockin genome editing strategy in HSPCs potently inhibits CCR5- and CXCR4-tropic HIV-1 infection

Amanda M. Dudek, William N. Feist, Elena J. Sasu et al. · Cell stem cell · 2024 · 15 citations · Full text

Medicine, Biotechnology, Hematology +17

A phase 1/2 open label nonrandomized clinical trial of intravenous 2-hydroxypropyl-β-cyclodextrin for acute liver disease in infants with Niemann-Pick C1

Margaret Reynolds, Laura Linneman, Sofia E. Luna et al. · Molecular Genetics and Metabolism Reports · 2021 · 12 citations · Full text

Medicine, Pediatrics, Pharmacology +17

Multilayered HIV-1 resistance in HSPCs through CCR5 Knockout and B cell secretion of HIV-inhibiting antibodies

William N. Feist, Sofia E. Luna, Kaya Ben-Efraim et al. · Nature Communications · 2025 · 12 citations · Full text

Life Sciences, Hematology, Immunology +17