Concepedia
Author
Philippine Aupy
Also Known As
6
Publications
276
Citations
H-Index
0
Concepts
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4
132
Palmitic acid conjugation enhances potency of tricyclo-DNA splice switching oligonucleotides
Karima Relizani, Lucía Echevarría, Faouzi Zarrouki, +11
Nucleic Acids Research
2021
41
Long-Term Efficacy of AAV9-U7snRNA-Mediated Exon 51 Skipping in mdx52 Mice
Philippine Aupy, Faouzi Zarrouki, Quentin Sandro, +6
Molecular Therapy — Methods & Clinical Development
2020
35
Evaluating the Impact of Variable Phosphorothioate Content in Tricyclo-DNA Antisense Oligonucleotides in a Duchenne Muscular Dystrophy Mouse Model
Lucía Echevarría, Philippine Aupy, Karima Relizani, +8
Nucleic Acid Therapeutics
2019
29
Identifying and Avoiding tcDNA-ASO Sequence-Specific Toxicity for the Development of DMD Exon 51 Skipping Therapy
Philippine Aupy, Lucía Echevarría, Karima Relizani, +8
Molecular Therapy — Nucleic Acids
27
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