Siham Ait Benichou

Antisense oligonucleotides as a potential treatment for brain deficits observed in myotonic dystrophy type 1

Siham Ait Benichou, Dominic Jauvin, Thiéry De Serres‐Bérard et al. · Gene Therapy · 2022 · 45 citations · Full text

Life Sciences, Neurology, Neuroscience +12

Enhanced Delivery of Ligand-Conjugated Antisense Oligonucleotides (C16-HA-ASO) Targeting Dystrophia Myotonica Protein Kinase Transcripts for the Treatment of Myotonic Dystrophy Type 1

Siham Ait Benichou, Dominic Jauvin, Thiéry De Serres‐Bérard et al. · Human Gene Therapy · 2022 · 23 citations

Medicine, Molecular Biology, Molecular Medicine +16

Lymphoblastoids cell lines – Derived iPSC line from a 26-year-old myotonic dystrophy type 1 patient carrying (CTG) 200 expansion in the DMPK gene: CHUQi001-A

Laurie Martineau, Véronique Racine, Siham Ait Benichou et al. · Stem Cell Research · 2017 · 17 citations · Full text

Life Sciences, Cell Biology, Genetics +11