Ubaldo Del Carro

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

Alessandra Biffi, Eugenio Montini, Laura Lorioli et al. · Science · 2013 · 1.2K citations · Full text

Life Sciences, Genetics, Hematology +16

Injection of adult neurospheres induces recovery in a chronic model of multiple sclerosis

Stefano Pluchino, Angelo Quattrini, Elena Brambilla et al. · Nature · 2003 · 1.1K citations

Life Sciences, Neurology, Neuroscience +17

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial

Maria Sessa, Laura Lorioli, Francesca Fumagalli et al. · The Lancet · 2016 · 507 citations

Medicine, Hematology, Molecular Medicine +13

Correction of metachromatic leukodystrophy in the mouse model by transplantation of genetically modified hematopoietic stem cells

Alessandra Biffi, Michele De Palma, Angelo Quattrini et al. · Journal of Clinical Investigation · 2004 · 287 citations · Full text

Medicine, Neurobiology, Neuroscience +17

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access

Francesca Fumagalli, Valeria Calbi, Maria Grazia Natali Sora et al. · The Lancet · 2022 · 284 citations · Full text

Medicine, Hematology, Immunology +15