In vivo correction of anaemia in β-thalassemic mice by γPNA-mediated gene editing with nanoparticle delivery

Raman Bahal, Nicole McNeer, Elias Quijano, +19

Nature Communications

In utero nanoparticle delivery for site-specific genome editing

Adele S. Ricciardi, Raman Bahal, James S. Farrelly, +13

Nature Communications

Delivery technologies for women’s health applications

Kelsey L. Swingle, Adele S. Ricciardi, William H. Peranteau, +1

Nature Reviews Bioengineering

Delivery TechnologiesFemtechReproductive HealthGynecologyDigital Health +5

In vivo correction of cystic fibrosis mediated by PNA nanoparticles

Alexandra S. Piotrowski-Daspit, Christina Barone, Chun-Yu Lin, +12

Science Advances

Pna NpsEngineeringIn Vivo Gene TherapyGene DeliveryBiomedical Engineering +14

Methodologies for Metabolomics: Experimental Strategies and Techniques

Adele S. Ricciardi

The Yale Journal of Biology and Medicine

EngineeringMetabolomic ProfilingMolecular BiologyExperimental StrategiesMolecular Thermodynamics +19

The C-terminal extension of Lsm4 interacts directly with the 3′ end of the histone mRNP and is required for efficient histone mRNA degradation

Shawn M. Lyons, Adele S. Ricciardi, Andrew Guo, +2

RNA

Structural and biochemical studies of SLIP1–SLBP identify DBP5 and eIF3g as SLIP1-binding proteins

Holger von Moeller, Rachel S. Lerner, Adele S. Ricciardi, +3

Nucleic Acids Research

In utero delivery of targeted ionizable lipid nanoparticles facilitates in vivo gene editing of hematopoietic stem cells

Rohan Palanki, John S. Riley, Sourav K. Bose, +22

Proceedings of the National Academy of Sciences

In Vivo Gene TherapyMonogenic Blood DiseasesGene DeliveryBiomedical EngineeringFetal Hscs +18

Nanoparticles for delivery of agents to fetal lungs

Sarah Ullrich, Mollie Freedman-Weiss, Samantha L. Ahle, +11

Acta Biomaterialia

NanoparticlesNanomedicineEngineeringNanomaterialsNano-drug Delivery +3

Targeted Genome Modification via Triple Helix Formation

Adele S. Ricciardi, Nicole McNeer, Kavitha K. Anandalingam, +2

Methods in molecular biology

Genome ModificationNatural SciencesMolecular BiologyDna ReplicationGene Editing +2