Helena Escobar

Human satellite cells have regenerative capacity and are genetically manipulable

Andreas Marg, Helena Escobar, Sina Gloy et al. · Journal of Clinical Investigation · 2014 · 80 citations · Full text

Tissue Engineering, Regeneration, Engineering +24

Human muscle-derived CLEC14A-positive cells regenerate muscle independent of PAX7

Andreas Marg, Helena Escobar, Nikos Karaiskos et al. · Nature Communications · 2019 · 47 citations · Full text

mRNA-mediated delivery of gene editing tools to human primary muscle stem cells

Christian Stadelmann, Silvia Di Francescantonio, Andreas Marg et al. · Molecular Therapy — Nucleic Acids · 2022 · 37 citations · Full text

Full-length Dysferlin Transfer by the Hyperactive Sleeping Beauty Transposase Restores Dysferlin-deficient Muscle

Helena Escobar, Verena Schöwel, Simone Spuler et al. · Molecular Therapy — Nucleic Acids · 2016 · 32 citations · Full text

Engineering, In Vivo Gene Therapy, Genetics +20

Exon Skipping in a Dysf-Missense Mutant Mouse Model

Jakub Malcher, Leonie Victoria Heidt, Aurélie Goyenvalle et al. · Molecular Therapy — Nucleic Acids · 2018 · 25 citations · Full text