Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial

Selim Corbacioglu, Simone Cesaro, Maura Faraci, +32

The Lancet

TransplantationHepatologyHepatic Veno-occlusive DiseaseStem Cell TransplantationImmunology +6

A Syndrome with Congenital Neutropenia and Mutations in<i>G6PC3</i>

Kaan Boztuǧ, Giridharan Appaswamy, Angel Ashikov, +23

New England Journal of Medicine

Megadose transplantation of purified peripheral blood CD34+progenitor cells from HLA-mismatched parental donors in children

Rupert Handgretinger, Thomas Klingebiel, Peter Lang, +9

Bone Marrow Transplantation

HistocompatibilityTransplantationMegadose TransplantationHuman Leukocyte AntigenStem Cell Transplantation +10

The MLL recombinome of acute leukemias

Claus Meyer, Björn Schneider, Stephan M. Jakob, +33

Leukemia

Hematological MalignancyMixed-phenotype Acute LeukemiaHematologyMll RecombinomeMedicine +3

Adoptive Transfer of Epstein-Barr Virus (EBV) Nuclear Antigen 1–Specific T Cells As Treatment for EBV Reactivation and Lymphoproliferative Disorders After Allogeneic Stem-Cell Transplantation

Vanya Icheva, Simone Kayser, Daniel Wolff, +12

Journal of Clinical Oncology

Increasing Mixed Chimerism Is an Important Prognostic Factor for Unfavorable Outcome in Children With Acute Lymphoblastic Leukemia After Allogeneic Stem-Cell Transplantation: Possible Role For Pre-Emptive Immunotherapy?

Peter Bader, Hermann Kreyenberg, W Hoelle, +16

Journal of Clinical Oncology

Hematological MalignancyCell TherapyTransplantationOncologyMixed-phenotype Acute Leukemia +13

Defibrotide in the treatment of children with veno-occlusive disease (VOD): a retrospective multicentre study demonstrates therapeutic efficacy upon early intervention

Selim Corbacioglu, Johann Greil, Christina Peters, +12

Bone Marrow Transplantation

Pediatric EpidemiologyPediatricsVeno-occlusive DiseaseRetrospective Multicentre StudyMedicine +2

Mutations in sphingosine-1-phosphate lyase cause nephrosis with ichthyosis and adrenal insufficiency

Svjetlana Lovric, Sara Gonçalves, Heon Yung Gee, +61

Journal of Clinical Investigation

GeneticsRenal PathologySteroid-resistant Nephrotic SyndromePathologyMolecular Genetics +15

Application of multipotent mesenchymal stromal cells in pediatric patients following allogeneic stem cell transplantation

Ingo Müller, Sandra Kordowich, Christina Holzwarth, +6

Blood Cells Molecules and Diseases

Regenerative MedicineCell TherapyTransplantationDevelopmental BiologyMedicine +9

Initial presenting manifestations in 16,486 patients with inborn errors of immunity include infections and noninfectious manifestations

Julian Thalhammer, Gerhard Kindle, Alexandra Nieters, +305

Journal of Allergy and Clinical Immunology

VaccinationPrimary ImmunodeficiencyMaternal ImmunizationInborn ErrorsAutoimmune Disease +10