Robert Muni‐Lofra

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy

Jean K. Mah, Paula R. Clemens, Michela Guglieri et al. · JAMA Network Open · 2022 · 88 citations · Full text

Pharmacy, Pharmacotherapy, Clinical Pharmacology +12

Respiratory involvement in ambulant and non-ambulant patients with facioscapulohumeral muscular dystrophy

Sandra Moreira, Libby Wood, Debbie Smith et al. · Journal of Neurology · 2017 · 45 citations · Full text

Medicine, Internal Medicine, Pulmonary Function Testing +16

Validation of the North Star Assessment for Limb-Girdle Type Muscular Dystrophies

M. James, Lindsay N. Alfano, Robert Muni‐Lofra et al. · Physical Therapy · 2022 · 30 citations · Full text

Medicine, Neurology, Rehabilitation Medicine +17

Determining minimal clinically important differences in the Hammersmith Functional Motor Scale Expanded for untreated spinal muscular atrophy patients: An international study

Giorgia Coratti, Francesca Bovis, Maria Carmela Pera et al. · European Journal of Neurology · 2024 · 30 citations · Full text

Medicine, Biostatistics, Neurology +17

Pubertal induction in adolescents with DMD is associated with high satisfaction, gonadotropin release and increased muscle contractile surface area

Claire Wood, Kieren G. Hollingsworth, Eric Hughes et al. · European Journal of Endocrinology · 2020 · 27 citations · Full text

Medicine, Endocrinology, Pediatrics +17