Todd A. Derksen

Recombinant adeno-associated virus type 2, 4, and 5 vectors: Transduction of variant cell types and regions in the mammalian central nervous system

Beverly L. Davidson, Colleen S. Stein, Jason Heth et al. · Proceedings of the National Academy of Sciences · 2000 · 519 citations

Immunology, Striatal Injections, Gene Delivery +17

In Vivo Treatment of Hemophilia A and Mucopolysaccharidosis Type VII Using Nonprimate Lentiviral Vectors

Colleen S. Stein, Yubin Kang, Sybille L. Sauter et al. · Molecular Therapy · 2001 · 89 citations · Full text

Systemic and Central Nervous System Correction of Lysosomal Storage in Mucopolysaccharidosis Type VII Mice

Colleen S. Stein, Abdi Ghodsi, Todd A. Derksen et al. · Journal of Virology · 1999 · 78 citations · Full text

Systemic Hyperosmolality Improves β-Glucuronidase Distribution and Pathology in Murine MPS VII Brain Following Intraventricular Gene Transfer

Abdi Ghodsi, Colleen S. Stein, Todd A. Derksen et al. · Experimental Neurology · 1999 · 76 citations

Neurodegenerative Diseases, Experimental Neuropathology, β-Glucuronidase Distribution +6

Retinal Pathology and Function in a Cln3 Knockout Mouse Model of Juvenile Neuronal Ceroid Lipofuscinosis (Batten Disease)

Gail M. Seigel, Andrew Lotery, A. J. Kummer et al. · Molecular and Cellular Neuroscience · 2002 · 73 citations

Batten Disease, Ocular Disease, Retina +8