N. Matthew Ellinwood

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs

Katherine P. Ponder, John R. Melniczek, Lingfei Xu et al. · Proceedings of the National Academy of Sciences · 2002 · 169 citations · Full text

Derivation of adult canine intestinal organoids for translational research in gastroenterology

Lawrance C. Chandra, Dana C. Borcherding, Dawn D. Kingsbury et al. · BMC Biology · 2019 · 151 citations · Full text

Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes

N. Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris et al. · Molecular Therapy · 2010 · 137 citations · Full text

Replacing the Enzyme α- <scp>l</scp> -Iduronidase at Birth Ameliorates Symptoms in the Brain and Periphery of Dogs with Mucopolysaccharidosis Type I

Ashley D. Dierenfeld, Michael F. McEntee, Carole Vogler et al. · Science Translational Medicine · 2010 · 81 citations · Full text

A model of mucopolysaccharidosis IIIB (Sanfilippo syndrome type IIIB): <i>N</i>‐acetyl‐α‐D‐glucosaminidase deficiency in Schipperke dogs

N. Matthew Ellinwood, P. Wang, TM Skeen et al. · Journal of Inherited Metabolic Disease · 2003 · 74 citations