Aime K. Johnson

Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector

Sourav Choudhury, Anne F Harris, Damien J. Cabral et al. · Molecular Therapy · 2015 · 113 citations · Full text

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy

Sourav Choudhury, Zachary Fitzpatrick, Anne F Harris et al. · Molecular Therapy · 2016 · 113 citations · Full text

Therapeutic Response in Feline Sandhoff Disease Despite Immunity to Intracranial Gene Therapy

Allison M. Bradbury, J. Nicholas Cochran, Victoria J. McCurdy et al. · Molecular Therapy · 2013 · 86 citations · Full text

Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease

Victoria J. McCurdy, Hannah E. Rockwell, Julian Arthur et al. · Gene Therapy · 2014 · 78 citations

Neurodegenerative Diseases, Widespread Correction, Neurological Disorder +14

Sustained Normalization of Neurological Disease after Intracranial Gene Therapy in a Feline Model

Victoria J. McCurdy, Aime K. Johnson, Heather Gray‐Edwards et al. · Science Translational Medicine · 2014 · 70 citations · Full text