Marshall W. Huston

Correction of Murine Rag2 Severe Combined Immunodeficiency by Lentiviral Gene Therapy Using a Codon-optimized RAG2 Therapeutic Transgene

Niek P. van Til, Helen de Boer, Nomusa Mashamba et al. · Molecular Therapy · 2012 · 70 citations · Full text

Life Sciences, Immunology, Molecular Genetics +16

AAV2/6 Gene Therapy in a Murine Model of Fabry Disease Results in Supraphysiological Enzyme Activity and Effective Substrate Reduction

Makiko Yasuda, Marshall W. Huston, Silvère Pagant et al. · Molecular Therapy — Methods & Clinical Development · 2020 · 55 citations · Full text

Life Sciences, Genetics, Molecular Genetics +16

Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-optimized IL2RG Gene and Minimal Pretransplant Conditioning

Marshall W. Huston, Niek P. van Til, Trudi P. Visser et al. · Molecular Therapy · 2011 · 44 citations · Full text

Medicine, Immunology, Molecular Medicine +13

Magselectofection: an integrated method of nanomagnetic separation and genetic modification of target cells

Yolanda Sánchez-Antequera, Olga Mykhaylyk, Niek P. van Til et al. · Blood · 2011 · 42 citations · Full text

Life Sciences, Biotechnology, Cell Biology +14

Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

Merel Stok, Helen de Boer, Marshall W. Huston et al. · Molecular Therapy — Methods & Clinical Development · 2020 · 36 citations · Full text

Life Sciences, Genetics, Molecular Genetics +14