N. M. Wulffraat

<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1

S. Hacein-Bey-Abina, Christof von Kalle, Manfred Schmidt et al. · Science · 2003 · 3.6K citations

Life Sciences, Genetics, Immunology +17

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

Salima Hacein‐Bey‐Abina, Alexandrine Garrigue, Gary P. Wang et al. · Journal of Clinical Investigation · 2008 · 1.8K citations · Full text

Medicine, Molecular Genetics, Oncology +14

Sustained Correction of X-Linked Severe Combined Immunodeficiency by ex Vivo Gene Therapy

Salima Hacein‐Bey‐Abina, Frédérique Carlier, Cécile Bouneaud et al. · New England Journal of Medicine · 2002 · 1.1K citations · Full text

Medicine, Genetics, Immunology +17

Long-term survival and transplantation of haemopoietic stem cells for immunodeficiencies: report of the European experience 1968–99

Corinne Antoine, Susanna Müller, Andrew J. Cant et al. · The Lancet · 2003 · 574 citations

Medicine, Hematology, Immunology +16

Human adenylate kinase 2 deficiency causes a profound hematopoietic defect associated with sensorineural deafness

Chantal Lagresle‐Peyrou, Emmanuelle Six, Capucine Pïcard et al. · Nature Genetics · 2008 · 238 citations · Full text

Medicine, Hematology, Molecular Genetics +13