Irene Gil-Fariña

Recombinant AAV Integration Is Not Associated With Hepatic Genotoxicity in Nonhuman Primates and Patients

Irene Gil-Fariña, Raffaele Fronza, Christine Kaeppel et al. · Molecular Therapy · 2016 · 174 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +16

Phase I open label liver-directed gene therapy clinical trial for acute intermittent porphyria

Delia D’Avola, Esperanza López‐Franco, Bruno Sangro et al. · Journal of Hepatology · 2016 · 142 citations · Full text

Medicine, Molecular Medicine, Pharmacology +15

Development of a Liver-specific Tet-On Inducible System for AAV Vectors and Its Application in the Treatment of Liver Cancer

Lucía Vanrell, Marianna Di Scala, Laura Blanco et al. · Molecular Therapy · 2011 · 61 citations · Full text

Life Sciences, Molecular Biology, Oncology +15

In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model

Citra Nurfarah Zaini Mattar, Irene Gil-Fariña, Cecilia Rosales et al. · Molecular Therapy · 2017 · 52 citations · Full text

Medicine, Molecular Genetics, Obstetrics +15

Therapeutic expression of human clotting factors IX and × following adeno‐associated viral vector‐mediated intrauterine gene transfer in early‐gestation fetal macaques

Jerry Kok Yen Chan, Irene Gil-Fariña, Nuryanti Johana et al. · The FASEB Journal · 2018 · 31 citations · Full text

Medicine, Molecular Biology, Obstetrics +16