Maribeth Cherry

AAV2 Vector Harboring a Liver-Restricted Promoter Facilitates Sustained Expression of Therapeutic Levels of α-Galactosidase A and the Induction of Immune Tolerance in Fabry Mice

Robin J. Ziegler, Scott Lonning, Donna Armentano et al. · Molecular Therapy · 2003 · 135 citations

Optimization of Plasmid Vectors for High-Level Expression in Lung Epithelial Cells

Nelson S. Yew, Donna M. Wysokenski, Kathryn X. Wang et al. · Human Gene Therapy · 1997 · 117 citations

Immunology, Molecular Biology, High-level Expression +19

A Concentrated and Stable Aerosol Formulation of Cationic Lipid:DNA Complexes Giving High-Level Gene Expression in Mouse Lung

Simon J. Eastman, Michael Lukason, Jennifer D. Tousignant et al. · Human Gene Therapy · 1997 · 88 citations

New Formulation, Engineering, Molecular Biology +18

Correction of the Biochemical and Functional Deficits in Fabry Mice Following AAV8–mediated Hepatic Expression of α-galactosidase A

Robin J. Ziegler, Maribeth Cherry, Christine M. Barbon et al. · Molecular Therapy · 2006 · 87 citations · Full text

AAV8-Mediated Hepatic Expression of Acid Sphingomyelinase Corrects the Metabolic Defect in the Visceral Organs of a Mouse Model of Niemann–Pick Disease

Christine M. Barbon, Robin J. Ziegler, Chester Li et al. · Molecular Therapy · 2005 · 49 citations · Full text

Acute Lung Injury, Acid Sphingomyelinase Deficiency, Inflammatory Lung Disease +29