Tabatha R. Simmons

Lack of Toxicity in Nonhuman Primates Receiving Clinically Relevant Doses of an AAV9.U7snRNA Vector Designed to Induce <i>DMD</i> Exon 2 Skipping

Liubov V. Gushchina, E. Frair, N. Rohan et al. · Human Gene Therapy · 2021 · 39 citations · Full text

A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2

Kevin M. Flanigan, Tatyana A. Vetter, Tabatha R. Simmons et al. · Molecular Therapy — Methods & Clinical Development · 2022 · 31 citations · Full text

The first exon duplication mouse model of Duchenne muscular dystrophy: A tool for therapeutic development

Adeline Vulin, Nicolas Wein, Tabatha R. Simmons et al. · Neuromuscular Disorders · 2015 · 30 citations

Knockout Mouse, Developmental Biology, Mendelian Disorder +9

The ZZ Domain of Dystrophin in DMD: Making Sense of Missense Mutations

Adeline Vulin, Nicolas Wein, Dana M. Strandjord et al. · Human Mutation · 2013 · 29 citations · Full text

Missense Mutations, Molecular Regulation, Molecular Biology +16

Increasing Genotype-Phenotype Model Determinism: Application to Bivariate Reading/Language Traits and Epistatic Interactions in Language-Impaired Families

Tabatha R. Simmons, Judy F. Flax, Marco A. Azaro et al. · Human Heredity · 2010 · 28 citations · Full text

Genetics, Psycholinguistics, Genomics +20