Concepedia
Statistics
Publications
9
Citations
238
H-Index
Active since
2019
Affiliations
Sangamo BioSciences (United States)(Current)
University of California, San Francisco
University of California, Davis
UCSF Benioff Children's Hospital
Cytokinetics (United States)
Bettina M. Cockroft is an author at Sangamo BioSciences (United States) specializing in medicine, hematology, and hemostatic disorders.
Publications per year
2019–2024
A phase III trial of <i>tirasemtiv</i> as a potential treatment for amyotrophic lateral sclerosis
Jeremy M. Shefner, Merit Cudkowicz, Orla Hardiman et al. · Amyotrophic Lateral Sclerosis and Frontotemporal Degeneration · 2019 · 46 citations · Full text
Life Sciences, Neurology, Pharmacotherapy +17
Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A. Rudnicki, Jinsy Andrews, Tina Duong et al. · Neurotherapeutics · 2021 · 44 citations · Full text
Medicine, Pharmacology, Pharmacotherapy +13
Giroctocogene fitelparvovec gene therapy for severe hemophilia A: 104-week analysis of the phase 1/2 Alta study
Andrew D. Leavitt, Barbara A. Konkle, Kimo C. Stine et al. · Blood · 2023 · 40 citations · Full text
Medicine, Hematology, Pharmacotherapy +12
Updated Follow-up of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (SB-525) Gene Therapy in Adults with Severe Hemophilia a
Andrew D. Leavitt, Barbara A. Konkle, Kimo C. Stine et al. · Blood · 2020 · 23 citations
Medicine, Hematology, Translational Sciences +7
Updated Results of the Alta Study, a Phase 1/2 Study of Giroctocogene Fitelparvovec (PF-07055480/SB-525) Gene Therapy in Adults with Severe Hemophilia a
Nathan Visweshwar, Thomas J. Harrington, Andrew D. Leavitt et al. · Blood · 2021 · 19 citations
Medicine, Hematology, Translational Sciences +10
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