Concepedia
3
Publications
75
Citations
H-Index
2019
Active since
Affiliations
Solidus Biosciences (United States)(Current)
UCLA Health
RTI Health Solutions
Pfizer (United States)
Duke University
Annie Ganot is an author at Solidus Biosciences (United States).
Publications per year
2019–2023
Priorities when deciding on participation in early-phase gene therapy trials for Duchenne muscular dystrophy: a best–worst scaling experiment in caregivers and adult patients
Ryan S. Paquin, Ryan Fischer, Carol Mansfield et al. · Orphanet Journal of Rare Diseases · 2019 · 36 citations · Full text
Microdystrophin Expression as a Surrogate Endpoint for Duchenne Muscular Dystrophy Clinical Trials
Jeffrey S. Chamberlain, Melissa A. Robb, Serge Braun et al. · Human Gene Therapy · 2023 · 26 citations · Full text
Patients’ and caregivers’ maximum acceptable risk of death for non‐curative gene therapy to treat Duchenne muscular dystrophy
Holly L. Peay, Ryan Fischer, Brennan Mange et al. · Molecular Genetics & Genomic Medicine · 2021 · 13 citations · Full text
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