Alex Dorenbaum

Efficacy of sapropterin dihydrochloride (tetrahydrobiopterin, 6R-BH4) for reduction of phenylalanine concentration in patients with phenylketonuria: a phase III randomised placebo-controlled study

Harvey L. Levy, Andrzej Milanowski, Anupam Chakrapani et al. · The Lancet · 2007 · 311 citations

Pharmacy, Pharmacotherapy, Clinical Nutrition +6

Efficacy of Sapropterin Dihydrochloride in Increasing Phenylalanine Tolerance in Children with Phenylketonuria: A Phase III, Randomized, Double-Blind, Placebo-Controlled Study

Friedrich K. Trefz, Barbara K. Burton, Nicola Longo et al. · The Journal of Pediatrics · 2009 · 192 citations

Pharmacy, Pediatrics, Pharmacotherapy +7

The response of patients with phenylketonuria and elevated serum phenylalanine to treatment with oral sapropterin dihydrochloride (6<i>R</i>‐tetrahydrobiopterin): a phase II, multicentre, open‐label, screening study

Barbara K. Burton, Dorothy K. Grange, Andrzej Milanowski et al. · Journal of Inherited Metabolic Disease · 2007 · 171 citations

Pharmacy, Pharmacology, Pharmacotherapy +7

Safety and efficacy of 22 weeks of treatment with sapropterin dihydrochloride in patients with phenylketonuria

Phillip Lee, Eileen P. Treacy, Eric Crombez et al. · American Journal of Medical Genetics Part A · 2008 · 101 citations

Pharmacy, Pharmacology, Pharmacotherapy +13

Recovery of Malassezia pachydermatis from eight infants in a neonatal intensive care nursery

Mark LaRocco, Alex Dorenbaum, Ann Robinson et al. · The Pediatric Infectious Disease Journal · 1988 · 75 citations

Medicine, Microbiology, Pediatrics +12