Fabrizia Urbinati

Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells

Mark A. DeWitt, Wendy Magis, Nicolas Bray et al. · Science Translational Medicine · 2016 · 495 citations · Full text

Life Sciences, Genetics, Molecular Genetics +17

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

Megan D. Hoban, Gregory J. Cost, Matthew Mendel et al. · Blood · 2015 · 320 citations · Full text

Life Sciences, Genetics, Hematology +14

Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy

Alessandro Aiuti, Barbara Cassani, Grazia Andolfi et al. · Journal of Clinical Investigation · 2007 · 253 citations · Full text

Medicine, Genetics, Molecular Biology +17

CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells

Megan D. Hoban, Dianne Lumaquin, Caroline Y. Kuo et al. · Molecular Therapy · 2016 · 216 citations · Full text

Life Sciences, Molecular Biology, Molecular Genetics +17

Retroviral vector integration deregulates gene expression but has no consequence on the biology and function of transplanted T cells

Alessandra Recchia, Chiara Bonini, Zulma Magnani et al. · Proceedings of the National Academy of Sciences · 2006 · 186 citations · Full text

Life Sciences, Immunology, Molecular Biology +13