Sunita Goyal

Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

David Adams, Alejandra González‐Duarte, William O’Riordan et al. · New England Journal of Medicine · 2018 · 2.9K citations · Full text

Life Sciences, Molecular Biology, Pharmacology +14

A retrospective analysis of the potential impact of IgG antibodies to agalsidase β on efficacy during enzyme replacement therapy for Fabry disease

Bernard Bénichou, Sunita Goyal, Crystal Sung et al. · Molecular Genetics and Metabolism · 2008 · 102 citations

Life Sciences, Biochemistry, Enzymology +4

Routine sterile glove and instrument change at the time of abdominal wound closure to prevent surgical site infection (ChEETAh): a pragmatic, cluster-randomised trial in seven low-income and middle-income countries

Aaron B Andoh, Abantanga Atindaana Francis, Abdulhafiz A Abdulkarim et al. · The Lancet · 2022 · 66 citations · Full text

Medicine, Surgery, Infection Prevention +16

Initial Results from the BEACON Clinical Study: A Phase 1/2 Study Evaluating the Safety and Efficacy of a Single Dose of Autologous CD34+ Base Edited Hematopoietic Stem Cells (BEAM-101) in Patients with Sickle Cell Disease with Severe Vaso-Occlusive Crises

Ashish O. Gupta, Akshay Sharma, Haydar Frangoul et al. · Blood · 2024 · 16 citations

Life Sciences, Biotechnology, Hematology +16

Resolution of Serious Vaso-Occlusive Pain Crises and Reduction in Patient-Reported Pain Intensity: Results from the Ongoing Phase 1/2 HGB-206 Group C Study of LentiGlobin for Sickle Cell Disease (bb1111) Gene Therapy

Alexis A. Thompson, Mark C. Walters, Markus Y. Mapara et al. · Blood · 2020 · 15 citations

Medicine, Hematology, Gene Therapy +14