Camilo Breton

Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol

Lili Wang, Jeff Smith, Camilo Breton et al. · Nature Biotechnology · 2018 · 122 citations

Oxysterol, Liver Physiology, Meganuclease Targeting +7

Integrated vector genomes may contribute to long-term expression in primate liver after AAV administration

Jenny A. Greig, Kelly M. Martins, Camilo Breton et al. · Nature Biotechnology · 2023 · 119 citations · Full text

CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX–knockout mice

Lili Wang, Yang Yang, Camilo Breton et al. · Blood · 2019 · 83 citations · Full text

A mutation-independent CRISPR-Cas9–mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency

Lili Wang, Yang Yang, Camilo Breton et al. · Science Advances · 2020 · 65 citations · Full text

CRISPR/Cas9 directed to the Ube3a antisense transcript improves Angelman syndrome phenotype in mice

Ralf S. Schmid, Xuefeng Deng, Priyalakshmi Panikker et al. · Journal of Clinical Investigation · 2021 · 56 citations · Full text

Neurogenomics, Genetics, Genomic Mechanism +21