Concepedia
Author
Jason Skowronski
Also Known As
5
Publications
186
Citations
4
H-Index
0
Concepts
All Affiliations
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All Concepts
3
180
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
Annalisa Lattanzi, Joab Camarena, Premanjali Lahiri, +20
Science Translational Medicine
2021
150
One Year Follow-up on the First Patient Treated with Nula-Cel: An Autologous CRISPR/Cas9 Gene Corrected CD34+ Cell Product to Treat Sickle Cell Disease
David C. Shyr, Robert Lowsky, Weston P. Miller, +37
Blood
2023
20
Molecular dynamics of genome editing with CRISPR-Cas9 and rAAV6 virus in human HSPCs to treat sickle cell disease
Liwen Xu, Premanjali Lahiri, Jason Skowronski, +3
Molecular Therapy — Methods & Clinical Development
10
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