Leslie Nelson

Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Craig M. McDonald, Craig Campbell, Ricardo Erazo Torricelli et al. · The Lancet · 2017 · 455 citations · Full text

Medicine, Molecular Medicine, Neurology +9

Consensus Statement on Standard of Care for Congenital Muscular Dystrophies

Ching H. Wang, Carsten G. Bönnemann, A. Rutkowski et al. · Journal of Child Neurology · 2010 · 215 citations · Full text

Medicine, Neurology, Neuromuscular Disorders +9

The gross motor function measure™ is a valid and sensitive outcome measure for spinal muscular atrophy

Leslie Nelson, Hollis Owens, Linda S. Hynan et al. · Neuromuscular Disorders · 2006 · 90 citations

Medicine, Neurology, Neuroscience +16

Rasch analysis of clinical outcome measures in spinal muscular atrophy

Stefan Cano, Anna Mayhew, Allan M. Glanzman et al. · Muscle & Nerve · 2013 · 78 citations · Full text

Education, Neurology, Neuroscience +13

Evaluator Training and Reliability for SMA Global Nusinersen Trials

Allan M. Glanzman, Elena Mazzone, Sally Dunaway Young et al. · Journal of Neuromuscular Diseases · 2018 · 55 citations · Full text

Medicine, Neurology, Functional Movement Assessment +16