Marianne Carlon

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

Eric W.F.W. Alton, Jeffrey M. Beekman, A. Christopher Boyd et al. · Thorax · 2016 · 141 citations · Full text

Translational Medicine, Lung Gene Transfer, Viral Diagnostics +15

Efficient and stable transduction of dopaminergic neurons in rat substantia nigra by rAAV 2/1, 2/2, 2/5, 2/6.2, 2/7, 2/8 and 2/9

Anke Van der Perren, Jaan Toelen, Marianne Carlon et al. · Gene Therapy · 2011 · 93 citations

Neurophysiology, Dopaminergic Neurons, Medicine +14

Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing

Giulia Maule, Antonio Casini, Claudia Montagna et al. · Nature Communications · 2019 · 82 citations · Full text

FK506 reduces neuroinflammation and dopaminergic neurodegeneration in an α-synuclein-based rat model for Parkinson's disease

Anke Van der Perren, Francesca Macchi, Jaan Toelen et al. · Neurobiology of Aging · 2015 · 79 citations

Neurodegenerative Diseases, Neurobiology Of Disease, Degenerative Diseases +14

rAAV-CFTRΔR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice

Dragana Vidović, Marianne Carlon, Mélanie Faria da Cunha et al. · American Journal of Respiratory and Critical Care Medicine · 2015 · 68 citations · Full text