Deirdre McMenamin

A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice

Yang Yang, Lili Wang, Peter Bell et al. · Nature Biotechnology · 2016 · 555 citations · Full text

Medicine, Molecular Biology, Molecular Genetics +15

Hepatic Gene Transfer in Neonatal Mice by Adeno-Associated Virus Serotype 8 Vector

Lili Wang, Huan Wang, Peter Bell et al. · Human Gene Therapy · 2011 · 114 citations · Full text

Pharmacy, Genetics, Immunology +14

Comparative Study of Liver Gene Transfer With AAV Vectors Based on Natural and Engineered AAV Capsids

Lili Wang, Peter Bell, Suryanarayan Somanathan et al. · Molecular Therapy · 2015 · 106 citations · Full text

Medicine, Molecular Biology, Molecular Medicine +15

CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX–knockout mice

Lili Wang, Yang Yang, Camilo Breton et al. · Blood · 2019 · 86 citations · Full text

Life Sciences, Genetics, Molecular Genetics +14

A mutation-independent CRISPR-Cas9–mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency

Lili Wang, Yang Yang, Camilo Breton et al. · Science Advances · 2020 · 66 citations · Full text

Life Sciences, Genetics, Molecular Genetics +16