John F. Brandsema

Cerebral Arteriopathy in Children With Neurofibromatosis Type 1

David Rea, John F. Brandsema, Derek Armstrong et al. · PEDIATRICS · 2009 · 133 citations

Medicine, Neurology, Pediatrics +17

Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

Eugenio Mercuri, Juan J. Vílchez, Odile Boespflug‐Tanguy et al. · The Lancet Neurology · 2024 · 120 citations

Medicine, Pediatrics, Pharmacotherapy +7

A phase 3 randomized placebo-controlled trial of tadalafil for Duchenne muscular dystrophy

Ronald G. Victor, H. Lee Sweeney, Richard S. Finkel et al. · Neurology · 2017 · 73 citations · Full text

Pharmacy, Pharmacotherapy, Exercise Testing +12

In Vivo NADH Fluorescence Monitoring as an Assay for Cellular Damage in Photodynamic Therapy¶

Brian W. Pogue, Jonathan D. Pitts, Mary‐Ann Mycek et al. · Photochemistry and Photobiology · 2001 · 63 citations

Life Sciences, Biochemistry, Biophysics +17

Intrathecal Onasemnogene Abeparvovec for Sitting, Nonambulatory Patients with Spinal Muscular Atrophy: Phase I Ascending-Dose Study (STRONG)

Richard S. Finkel, Basil T. Darras, Jerry R. Mendell et al. · Journal of Neuromuscular Diseases · 2023 · 63 citations · Full text

Medicine, Neurology, Pharmacotherapy +13