Gareth Hazell

Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy

Suzan M. Hammond, Gareth Hazell, Fazel Shabanpoor et al. · Proceedings of the National Academy of Sciences · 2016 · 193 citations · Full text

Pharmacy, Neuroscience, Pharmacology +16

Identification of a Peptide for Systemic Brain Delivery of a Morpholino Oligonucleotide in Mouse Models of Spinal Muscular Atrophy

Fazel Shabanpoor, Suzan M. Hammond, Frank Abendroth et al. · Nucleic Acid Therapeutics · 2017 · 62 citations · Full text

Pharmacy, Neurology, Neuroscience +17

Interventions Targeting Glucocorticoid-Krüppel-like Factor 15-Branched-Chain Amino Acid Signaling Improve Disease Phenotypes in Spinal Muscular Atrophy Mice

Lisa Walter, Marc‐Olivier Deguise, Katharina E. Meijboom et al. · EBioMedicine · 2018 · 47 citations · Full text

Life Sciences, Neurobiology, Neuroscience +17

Combining multiomics and drug perturbation profiles to identify muscle-specific treatments for spinal muscular atrophy

Katharina E. Meijboom, Viola Volpato, Jimena Monzón‐Sandoval et al. · JCI Insight · 2021 · 20 citations · Full text

Life Sciences, Neurobiology, Neuroscience +17

Light modulation ameliorates expression of circadian genes and disease progression in spinal muscular atrophy mice

Lisa Walter, Christiane E. Koch, Corinne Betts et al. · Human Molecular Genetics · 2018 · 15 citations · Full text

Life Sciences, Neurology, Neuroscience +17