Мilan Petakov

Pivotal trial with plant cell–expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease

Ari Zimran, Einat Brill‐Almon, Raul Chertkoff et al. · Blood · 2011 · 205 citations · Full text

Life Sciences, Plant Sciences, Glycobiology +13

Effect of Oral Eliglustat on Splenomegaly in Patients With Gaucher Disease Type 1

Pramod K. Mistry, Elena Lukina, Hadhami Ben Turkia et al. · JAMA · 2015 · 156 citations

Medicine, Hematology, Pharmacotherapy +11

Oxidised low-density lipoprotein concentration – early marker of an altered lipid metabolism in young women with PCOS

Svetozar Damjanović, Dimitrios Panidis, Nikolaos Spanos et al. · European Journal of Endocrinology · 2006 · 103 citations · Full text

Medicine, Endocrinology, Gynecology +17

Outcomes after 18 months of eliglustat therapy in treatment‐naïve adults with <scp>G</scp>aucher disease type 1: The phase 3 ENGAGE trial

Pramod K. Mistry, Elena Lukina, Hadhami Ben Turkia et al. · American Journal of Hematology · 2017 · 99 citations · Full text

Medicine, Clinical Pharmacokinetics, Hematology +13

Peripheral neuropathy in adult type 1 Gaucher disease: a 2-year prospective observational study

Marieke Biegstraaten, Eugen Mengel, László Maródi et al. · Brain · 2010 · 87 citations · Full text

Medicine, Internal Medicine, Neurology +15