Felicia Migone

Long-Term Efficacy after [E1 ^- , polymerase ^- ] Adenovirus-Mediated Transfer of Human Acid-α-Glucosidase Gene into Glycogen Storage Disease Type II Knockout Mice

Enyu Ding, Bradley L. Hodges, Hsun‐Ming Hu et al. · Human Gene Therapy · 2001 · 63 citations

Efficacy of Gene Therapy for a Prototypical Lysosomal Storage Disease (GSD-II) Is Critically Dependent on Vector Dose, Transgene Promoter, and the Tissues Targeted for Vector Transduction

Enyu Ding, Huimin Hu, Bradley L. Hodges et al. · Molecular Therapy · 2002 · 63 citations · Full text

Improved efficacy of gene therapy approaches for Pompe disease using a new, immune-deficient GSD-II mouse model

Fang Xu, Enyu Ding, SX Liao et al. · Gene Therapy · 2004 · 39 citations

Knockout Mouse, Pompe Disease, Immunogenetics +11

Glycogen storage in multiple muscles of old GSD-II mice can be rapidly cleared after a single intravenous injection with a modified adenoviral vector expressing hGAA

Fang Xu, Enyu Ding, Felicia Migone et al. · The Journal of Gene Medicine · 2005 · 31 citations

Multiple muscles in the AMD quail can be “cross‐corrected” of pathologic glycogen accumulation after intravenous injection of an [E1‐, polymerase‐] adenovirus vector encoding human acid‐α‐glucosidase

Alison McVie‐Wylie, Enyu Ding, Terrence A. Lawson et al. · The Journal of Gene Medicine · 2002 · 17 citations