Haematopoietic stem cell transplantation trends in children over the last three decades: a survey by the paediatric diseases working party of the European Group for Blood and Marrow Transplantation

Maurizio Miano, Myriam Labopin, Olivier Hartmann, +15

Bone Marrow Transplantation

TransplantationMarrow TransplantationBone Marrow FailurePediatric HematologyPaediatric Diseases +7

Risk of complications during hematopoietic stem cell collection in pediatric sibling donors: a prospective European Group for Blood and Marrow Transplantation Pediatric Diseases Working Party study

Jan Styczyński, Adriana Balduzzi, Lidia Gil, +21

Blood

Hyperactive mTOR pathway promotes lymphoproliferation and abnormal differentiation in autoimmune lymphoproliferative syndrome

Simon Völkl, Anne Rensing‐Ehl, Andrea Allgäuer, +21

Blood

Very late nonfatal consequences of fractionated TBI in children undergoing bone marrow transplant

Maura Faraci, Salvina Barra, Amnon Cohen, +13

International Journal of Radiation Oncology*Biology*Physics

TransplantationBone Marrow FailureFractionated TbiPediatric HematologyBone Marrow Transplant +7

Outcomes and Treatment Strategies for Autoimmunity and Hyperinflammation in Patients with RAG Deficiency

Jocelyn R. Farmer, Zsófia Földvári, Boglárka Ujházi, +70

The Journal of Allergy and Clinical Immunology In Practice

Outcome of haematopoietic stem cell transplantation in dyskeratosis congenita

Francesca Fioredda, Simona Iacobelli, Elisabeth T Korthof, +29

British Journal of Haematology

TransplantationMarrow TransplantationAutoimmune DiseaseBone Marrow FailureDyskeratosis Congenita +12

Four year follow-up of a case of fucosidosis treated with unrelated donor bone marrow transplantation

Maurizio Miano, Edoardo Lanino, R. Gatti, +6

Bone Marrow Transplantation

TransplantationMarrow TransplantationBone Marrow FailureTransplantation MedicineHematology +2

Mycophenolate mofetil and Sirolimus as second or further line treatment in children with chronic refractory Primitive or Secondary Autoimmune Cytopenias: a single centre experience

Maurizio Miano, Maria Scalzone, Katia Perri, +10

British Journal of Haematology

ImmunodeficienciesImmunologyImmunotherapySingle Centre ExperienceMmf Therapy +20

Defects in mitochondrial energetic function compels Fanconi Anaemia cells to glycolytic metabolism

Enrico Cappelli, Paola Cuccarolo, Giorgia Stroppiana, +5

Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease

MitophagyMitochondrial FunctionBiochemistryOrganelle DynamicPhysiology +7

Megatherapy combining I131 metaiodobenzylguanidine and high-dose chemotherapy with haematopoietic progenitor cell rescue for neuroblastoma

Maurizio Miano, Alberto Garaventa, MR Pizzitola, +6

Bone Marrow Transplantation

Hematological MalignancyMedicineCell Replacement TherapyI131 MetaiodobenzylguanidineHigh-dose Chemotherapy +7