Heidi Elliot

Betibeglogene Autotemcel Gene Therapy for Non–β ⁰ /β ⁰ Genotype β-Thalassemia

Franco Locatelli, Alexis A. Thompson, Janet L. Kwiatkowski et al. · New England Journal of Medicine · 2021 · 237 citations · Full text

HYPERCALCAEMIC OSTEOMALACIA DUE TO ALUMINIUM TOXICITY

B.F. Boyce, H. Y. Elder, Heidi Elliot et al. · The Lancet · 1982 · 166 citations

Bone Disease, Bone Health, Osteoporosis +2

Betibeglogene autotemcel gene therapy in patients with transfusion-dependent, severe genotype β-thalassaemia (HGB-212): a non-randomised, multicentre, single-arm, open-label, single-dose, phase 3 trial

Janet L. Kwiatkowski, Mark C. Walters, Suradej Hongeng et al. · The Lancet · 2024 · 31 citations

Translational Medicine, Cell Therapy, Health Sciences +8

Northstar-3: Interim Results from a Phase 3 Study Evaluating Lentiglobin Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia and Either a β0 or IVS-I-110 Mutation at Both Alleles of the HBB Gene

Ashutosh Lal, Franco Locatelli, Janet L. Kwiatkowski et al. · Blood · 2019 · 25 citations

Northstar-2: Updated Safety and Efficacy Analysis of Lentiglobin Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia and Non-β0/β0 Genotypes

Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski et al. · Blood · 2019 · 14 citations