Publication | Open Access
Safety, tolerability and pharmacokinetics of eteplirsen in young boys aged 6–48 months with Duchenne muscular dystrophy amenable to exon 51 skipping
21
Citations
37
References
2023
Year
Duchenne Muscular DystrophyPediatricsPharmacotherapyYoung BoysMedicineNeuromusculoskeletal Disorder
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