The French Compassionate Program of elexacaftor-tezacaftor-ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del<i>CFTR</i>variant - Concepedia

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The French Compassionate Program of elexacaftor-tezacaftor-ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del<i>CFTR</i>variant

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References

2023

Year

Pierre‐Régis Burgel, Isabelle Sermet‐Gaudelus, I. Durieu, Reem Kanaan, Julie Macey, Dominique Grenet, Michele Porzio, Nathalie Coolen-Allou, R. Chiron, Christophe Marguet,

European Respiratory Journal

Abstract

Clinical benefits were observed in a large subset of people with CF with advanced lung disease and <i>CFTR</i> variants not currently approved for ETI.