Concepedia

Publication | Open Access

Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities

DOIFull Paper Access

13

Citations

35

References

2022

Year

Suhail Khoja, Jenna Lambert, Matthew Nitzahn, Adam Eliav, Yuchen Zhang, Mikayla Tamboline, Colleen T. Le, Eram Nasser, Yunfeng Li, Puja Patel,
Molecular Therapy — Methods & Clinical Development

References

YearCitations

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