Concepedia

Premature delivery in the domestic sow in response to in utero delivery of AAV9 to fetal piglets

Kelly Rich, Christopher G. Wier, Jessica Russo, Lingling Kong, Patrick L. Heilman, Anthony Reynolds, Amy Knapp, Megan G. Pino, Elizabeth Keckley, Lori Mattox,

Gene Therapy · 2021 · 11 citations · 43 references

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References

43

Identification and characterization of a spinal muscular atrophy-determining gene

Suzie Lefebvre, Lydie Bürglen, Sophie Reboullet et al. · Cell · 1995 · 4K citations · Full text

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Global, regional, and national causes of child mortality in 2000–13, with projections to inform post-2015 priorities: an updated systematic analysis

Li Liu, Shefali Oza, Daniel Hogan et al. · The Lancet · 2014 · 3.2K citations

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Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy

Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text

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Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy

Richard S. Finkel, Eugenio Mercuri, Basil T. Darras et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text

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Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes

Kevin D. Foust, Emily Nurre, Chrystal L. Montgomery et al. · Nature Biotechnology · 2008 · 1.4K citations · Full text

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