Nusinersen treatment of Spinal Muscular Atrophy Type 1 — results of expanded access programme in Poland - Concepedia

Concepedia

Publication | Open Access

Nusinersen treatment of Spinal Muscular Atrophy Type 1 — results of expanded access programme in Poland

DOI Full Paper Access

25

Citations

16

References

2021

Year

Sandra Modrzejewska, Katarzyna Kotulska, Ilona Kopyta, Ewa Grędowska, Ewa Emich‐Widera, Katarzyna Tomaszek, Justyna Paprocka, Dariusz Chmielewski, Jacek Pilch, Jerzy Pietruszewski,

Neurologia i Neurochirurgia Polska

Abstract

Our data indicates that nusinersen treatment might be effective in SMA type 1 patients, regardless of their age and functional status.

References

	Year	Citations

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