European Spine Journal · 2020 · 29 citations · 14 references
MedicineOrthopedic SurgeryRehabilitation MedicinePhysical TherapyPulmonary RehabilitationSpine SurgeryGrowth AssessmentPediatric OrthopedicsPreoperative Pulmonary RehabilitationSpinal Muscular AtrophySpine RehabilitationStrengthening ExercisesLung GrowthMuscle AtrophyMuscle GrowthOrthopedic Growth ModificationSpinal Muscular Atrophy RehabilitationSpinal Muscular Atrophy-associated Scoliosis
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Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy
Jerry R. Mendell, Samiah Al-Zaidy, Richard Shell et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Richard S. Finkel, Eugenio Mercuri, Basil T. Darras et al. · New England Journal of Medicine · 2017 · 2.3K citations · Full text
Spinal Muscular Atrophy: Natural History and Orthopaedic Treatment of Scoliosis
C Granata, Luciano Merlini, Elisabetta Magni et al. · Spine · 1989 · 104 citations
Growing Rods for Scoliosis in Spinal Muscular Atrophy
Mark J. McElroy, Adam C. Shaner, Thomas O. Crawford et al. · Spine · 2011 · 102 citations