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How long does gene therapy last? 4-year follow-up of phase 3 voretigene neparvovec trial in RPE65-associated LCA/inherited retinal disease

Arlene V. Drack, Jean Bennett, Stephen R. Russell, Katherine A. High, Zi‐Fan Yu, Amy Tillman, Daniel C. Chung, Kathleen Z. Reape, Thomas A. Ciulla, Albert Maguire

Journal of American Association for Pediatric Ophthalmology and Strabismus · 2019 · 20 citations · 0 references

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